uniQure’s Post

As with other medicinal products, the success rate of ATMP products reaching commercialization is often lower than desired, if not worse. One critical factor for improving success is having a deep understanding of product critical quality attributes (CQAs) and critical process parameters (CPPs). Join us in this session as we take a deep dive into the discovery and development of advanced therapy medicinal products (ATMPs), sharing experiences and insights to improve the success rate of ATMP product commercialization. We'll also delve into the specific topic of lifecycle management and comparability of AAV gene therapy, using real-world examples to illustrate best practices. Don't miss out on this valuable opportunity to enhance your understanding of ATMPs and their commercialization potential.

Is functional supply chain logistics (SCL) in your cell or gene therapy trial keeping you up at night? Whether it be concerns about the high cost of 3rd party SCL management technology, quality concerns over having insufficient staff capable of executing and managing a SCL program, or just the risks associated with lacking an integrated technical capability, Clinscience has the solution. Learn more about our proprietary SCL platform launching this fall, contact us at contact@clinscience.com #sclmanagement #celltherapy #genetherapy #clinicaltrialworries #costconcerns #supplychain #oncology #cellandgenetherapy #clinicaltrials #pharma #biotech

Science spotlight: New class of molecular glues, gene therapy for FTD/ALS and more - BioCentury >>> lqventures.com #strategy #competitiveintelligence #marketing #biotech #competitivemarketing #pharmaceutical #healthcare #pharma

Science spotlight: New class of molecular glues, gene therapy for FTD/ALS and more - BioCentury >>> lqventures.com #strategy #competitiveintelligence #marketing #healthcare #competitivemarketing #pharma #pharmaceutical #biotech

The November issue of Life Science Leader is out! Krish Krishnan and Suma Krishnan of (Pittsburgh-based) Krystal Biotech, Inc. are on the cover, sharing details of their journey to bring the first topical, redosable gene therapy to market. Sath Shukla talks about Spero Therapeutics' business model for novel antibiotics, Wayne Koberstein covers Freya Biosciences in 'Companies To Watch,' and more: https://lnkd.in/gggauDAb.

Exploring Alignment in Transfection Reagent Release Standards: Insights from BioPhorum Discover a Quality by Design perspective as experts from leading bio/pharmaceutical companies, including our own Andrew Schaefer, MBA, delve into the identification of crucial attributes within the cell and gene therapy manufacturing process. Dive into the comprehensive article for insights into the regulatory landscape, material characteristics, and test requirements. Explore topics such as defining quality target material profiles and attributes, establishing a product control strategy, and identifying critical material attributes. Read the full article ➡️ https://buff.ly/3uAerD4 Learn more ➡️ https://buff.ly/46yPMvL #eurofins #biopharma #celltherapy #genetherapy  

Discover what challenges lie ahead of the Cell and Gene Therapy industry 🧬. Benefit from proven working methods that will help you succeed - and increase your speed to market - in this interview with Dr. Judith K.. Our Senior Industry Advisor and Principal Consultant Advanced Therapies, at Körber Pharma #Software, offers an overview and best practices of the iterative approach to a digital therapy process. Find out more about unlocking the potential of your cell and gene manufacturing! Watch the full interview here 👉 https://lnkd.in/dsy3cBQs. #KörberPharma #pharma #cellandgenetherapy #Körber #cellandgene

💡 Want to navigate the complexities of Cell and Gene Therapy development? Our webinar series has you covered! Learn how to create a holistic CMC plan and optimize your process for success. Register today! https://buff.ly/4dWVyMS #GeneTherapy #Pharma #BioTech

Thoughts on this? >> Neurogene a new outperform at Baird on gene therapy for Rett syndrome - Seeking Alpha >> Comment below! >>> lqventures.com #strategy #competitiveintelligence #marketing #pharmaceutical #competitivemarketing #biotech #healthcare #pharma

Supply chain disruptions continue to plague the biopharma industry, but collaboration is key to building a more stable future. The year ahead is likely to bring advancements in manufacturing technology and automation that ill significantly impact cell and gene therapy production. How can we strengthen collaboration across the biopharma ecosystem to ensure a steady supply of critical medicines?     Discover more: https://lnkd.in/g2AgsfdD    #biopharma #supplychain #collaboration #resilience