💡 Discover AIT-101: OrphAI Therapeutics' groundbreaking treatment for ALS has now earned Orphan Drug Designation in the EU! With its unique ability to clear toxic aggregates, AIT-101 is leading the charge against ALS, offering hope to patients worldwide. https://lnkd.in/e3rTq-K6
About us
At OrphAI Therapeutics, we are focused on identifying and developing innovative therapeutics. Our current clinical stage drug candidates target Group 1 and Group 3 Pulmonary Hypertension and bronchiolitis obliterans syndrome post lung transplant.
- Website
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https://www.orphai-therapeutics.com
External link for OrphAI Therapeutics
- Industry
- Biotechnology Research
- Company size
- 2-10 employees
- Headquarters
- Guilford
- Type
- Privately Held
- Founded
- 2013
- Specialties
- clinical development, molecular and cell biology, pulmonary hypertension, and bronchiolitis obliterans syndrome post lung transplant
Locations
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Primary
Get directions
530 Whitfield St.
Guilford, 06437, US
Employees at OrphAI Therapeutics
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Paul Boni
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Jonathan Rothberg
#ThanksObama - email joinus@4Catalyzer.com to help save the life of someone you love. Follow me on Twitter @JMRothberg
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Jay Fine
President, Research and Development at EvolveImmune Therapeutics; Independent Board Director
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David Rosenthal M.D.
Healthcare advisor, investor, and entrepreneur. Physician & Faculty @Yale | Venture Partner @ Alleycorp | Former Chief Medical Officer @Tesseract…
Updates
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OrphAI Therapeutics has been granted Orphan Drug Designation by the EU for AIT-101, aimed at treating amyotrophic lateral sclerosis (ALS). Following its US FDA approval, this marks a significant step toward battling this neurodegenerative disease. https://lnkd.in/e3rTq-K6
OrphAI Therapeutics receives Orphan Drug Designation for AIT-101 as a treatment for amyotrophic lateral sclerosis in the European Union
globenewswire.com
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OrphAI Therapeutics Appoints Jay Fine, PhD to Board of Directors https://lnkd.in/eBCDRbru
OrphAI Therapeutics Announces Appointment of Jay Fine to Board of Directors
globenewswire.com
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We have grown into a clinically focused company with a mission to bring life-saving drugs to patients with rare diseases. Our new name, OrphAI Therapeutics, echoes our progress & our legacy in leveraging AI for drug development." - Brigette Roberts, CEO of OrphAI Therapeutics. https://lnkd.in/gX5gKkVF
AI Therapeutics Announces Name Change to OrphAI Therapeutics
globenewswire.com
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OrphAI Therapeutics will be at the 22nd Annual NEALS (Northeast ALS Consortium) meeting being held October 4 - 6, 2023 in Clearwater Florida. https://lnkd.in/gCPg_Mek
OrphAI Therapeutics Announces Oral Presentation and Posters at the 22nd Annual NEALS Conference
globenewswire.com
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AI Therapeutics is now OrphAI Therapeutics Inc. This rebrand signifies our sharpened focus on developing treatments for orphan diseases. https://lnkd.in/gX5gKkVF
AI Therapeutics Announces Name Change to OrphAI Therapeutics
globenewswire.com
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Exciting News! AI Therapeutics has rebranded to OrphAI Therapeutics Inc. as we further our commitment to treating rare diseases. Our new name captures our evolution & dedication to those in need. https://lnkd.in/gX5gKkVF
AI Therapeutics Announces Name Change to OrphAI Therapeutics
globenewswire.com
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Our 24-week study aims to evaluate LAM-001's safety, tolerability, and efficacy in 15 adults with advanced PAH. Primary endpoints include changes in peak oxygen uptake, among other hemodynamic metrics. https://lnkd.in/gJb4fcEg
AI Therapeutics Announces Initiation of a Phase 2 Clinical Trial of LAM-001 for Treatment of Pulmonary Arterial Hypertension (PAH)
globenewswire.com
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What sets LAM-001 apart? Dr. Aaron Waxman, Principal Investigator, explains: "Unlike current therapies, LAM-001 addresses the cellular remodeling that is the root cause of PAH by modulating both the mTOR and BMPR2 pathways." https://lnkd.in/gJb4fcEg
AI Therapeutics Announces Initiation of a Phase 2 Clinical Trial of LAM-001 for Treatment of Pulmonary Arterial Hypertension (PAH)
globenewswire.com
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Exciting News! AI Therapeutics has initiated a Phase II study for LAM-001, a novel inhaled form of sirolimus, aimed at treating Pulmonary Arterial Hypertension (PAH) — a life-threatening condition affecting 30,000 U.S. patients. https://lnkd.in/gJb4fcEg