CGTLive

CGTLive took a look at the road #leukodystrophy gene therapies have faced to approval and their current state. Learn more about it now, featuring insights from Dr. Alessandro Aiutti from Ospedale San Raffaele and Dr. Maria Escolar from ForgeBio https://lnkd.in/ePTU8vXZ

ICYMI: Jacques Galipeau, MD, Don and Marilyn Anderson Professor of Oncology at University of Wisconsin – Madison discussed the state of cell and gene therapy development. Watch now: https://lnkd.in/gTWqqG2T

ICYMI: The FDA has cleared IASO Bio’s IND application for its CAR T-cell therapy equecabtagene autoleucel for the potential treatment of #multiplesclerosis. Read more now: https://lnkd.in/g62aVAKG

ICYMI: The AFFINE study also met key secondary endpoints. #Hemophilia #HemophiliaA #genetherapy Pfizer Read more: https://lnkd.in/ePV3SXVp

“[UMGD] I think, is one of the very few technologies that can do that.” -Carol Miao, PhD (Seattle Children's) #ASGCT2024 #genetherapy #HemophiliaA Watch: https://lnkd.in/emJfd4V3

ICYMI: The therapy is Anixa’s modified CAR T-cell therapy approach using an endocrine receptor (FSHR) as the target of the engineered T-cells. #ovca #ovariancancer #celltherapy Anixa Biosciences, Inc. Read more: https://lnkd.in/e8eJdZjG

DiscGenics anticipates that the first patient in PIVOT will be enrolled within the fourth quarter of this year. #celltherapy #DegenerativeDiscDisease #SpineSurgery Read more: https://lnkd.in/e2Mah_eT

The AFFINE study also met key secondary endpoints. #Hemophilia #HemophiliaA #genetherapy Pfizer Read more: https://lnkd.in/ePV3SXVp

ICYMI: The OIG explained its unfavorable opinion, stating that it did not have the necessary data to determine the program’s risk of fraud and abuse and therefore grant it immunity to the federal antikickback statute. bluebird bio #genetherapy #SickleCell More: https://lnkd.in/e2huNGJb

The FDA has cleared IASO Bio’s IND application for its CAR T-cell therapy equecabtagene autoleucel for the potential treatment of #multiplesclerosis. Read more now. https://lnkd.in/g62aVAKG