RNA modifications in physiology and disease: towards clinical applications

S Delaunay, M Helm, M Frye�- Nature Reviews Genetics, 2024 - nature.com
The ability of chemical modifications of single nucleotides to alter the electrostatic charge,
hydrophobic surface and base pairing of RNA molecules is exploited for the clinical use of�…

[HTML][HTML] Autism spectrum disorder: neurodevelopmental risk factors, biological mechanism, and precision therapy

L Wang, B Wang, C Wu, J Wang, M Sun�- International journal of�…, 2023 - mdpi.com
Autism spectrum disorder (ASD) is a heterogeneous, behaviorally defined
neurodevelopmental disorder. Over the past two decades, the prevalence of autism�…

Antisense oligonucleotide rescue of CGG expansion–dependent FMR1 mis-splicing in fragile X syndrome restores FMRP

S Shah, KJ Sharp, S Raju Ponny…�- Proceedings of the�…, 2023 - National Acad Sciences
Aberrant alternative splicing of mRNAs results in dysregulated gene expression in multiple
neurological disorders. Here, we show that hundreds of mRNAs are incorrectly expressed�…

[HTML][HTML] Elevated levels of FMRP-target MAP1B impair human and mouse neuronal development and mouse social behaviors via autophagy pathway

Y Guo, M Shen, Q Dong, NM M�ndez-Albelo…�- Nature�…, 2023 - nature.com
Fragile X messenger ribonucleoprotein 1 protein (FMRP) binds many mRNA targets in the
brain. The contribution of these targets to fragile X syndrome (FXS) and related autism�…

[HTML][HTML] Neuropathology of incidental Lewy body & prodromal Parkinson's disease

T Koeglsperger, SL Rumpf, P Schlie�er…�- Molecular�…, 2023 - Springer
Background Parkinson's disease (PD) is a progressive neurodegenerative disorder
associated with a loss of dopaminergic (DA) neurons. Despite symptomatic therapies, there�…

[HTML][HTML] Codon optimality-mediated mRNA degradation: Linking translational elongation to mRNA stability

H Bae, J Coller�- Molecular cell, 2022 - cell.com
Messenger RNA (mRNA) translation by the ribosome represents the final step of a
complicated molecular dance from DNA to protein. Although classically considered a�…

mRNA transport, translation, and decay in adult mammalian central nervous system axons

J Jung, J Ohk, H Kim, CE Holt, HJ Park, H Jung�- Neuron, 2023 - cell.com
Localized mRNA translation regulates synapse function and axon maintenance, but how
compartment-specific mRNA repertoires are regulated is largely unknown. We developed an�…

Aberrant hyperexpression of the RNA binding protein FMRP in tumors mediates immune evasion

Q Zeng, S Saghafinia, A Chryplewicz, N Fournier…�- Science, 2022 - science.org
Many human cancers manifest the capability to circumvent attack by the adaptive immune
system. In this work, we identified a component of immune evasion that involves frequent up�…

Species-specific FMRP regulation of RACK1 is critical for prenatal cortical development

M Shen, CL Sirois, Y Guo, M Li, Q Dong…�- Neuron, 2023 - cell.com
Fragile X messenger ribonucleoprotein 1 protein (FMRP) deficiency leads to fragile X
syndrome (FXS), an autism spectrum disorder. The role of FMRP in prenatal human brain�…

De novo variants in genes regulating stress granule assembly associate with neurodevelopmental disorders

X Jia, S Zhang, S Tan, B Du, M He, H Qin, J Chen…�- Science�…, 2022 - science.org
Stress granules (SGs) are cytoplasmic assemblies in response to a variety of stressors. We
report a new neurodevelopmental disorder (NDD) with common features of language�…